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EP About this file: EP4288556

EP4288556 - METHODS FOR PREVENTING CARDIAC OR SKELETAL DEFECTS IN DISEASES INCLUDING MUCOPOLYSACCHARIDOSES [Right-click to bookmark this link]
StatusRequest for examination was made
Status updated on  10.11.2023
Database last updated on 14.09.2024
FormerThe international publication has been made
Status updated on  12.08.2022
Formerunknown
Status updated on  11.03.2022
Most recent event   Tooltip15.06.2024New entry: Decision on request for further processing 
Applicant(s)For all designated states
Regents of the University of Minnesota
600 McNamara Alumni Center
200 Oak Street SE
Minneapolis, Minnesota 55455-2020 / US
For all designated states
REGENXBIO Inc.
9804 Medical Center Drive
Rockville, MD 20850 / US
[2023/50]
Inventor(s)01 / MCIVOR, R., Scott
Louis Park, Minnesota 55416 / US
02 / BUSS, Nicholas, Alexander, Piers, Sascha
Rockville, Maryland 20852 / US
03 / LUND, Troy, C.
Eden Prairie, Minnesota 55347 / US
04 / BRAUNLIN, Elizabeth
Roseville, Minnesota 55113 / US
05 / BELUR, Lalitha, R.
St. Paul, Minnesota 55116 / US
06 / FAIRBANKS, Carolyn
St. Paul, Minnesota 55105 / US
07 / NEVORET, Marie-Laure
Virgina Beach, Virginia 23452 / US
 [2023/50]
Representative(s)Forresters IP LLP
Skygarden
Erika-Mann-Straße 11
80636 München / DE
[2023/50]
Application number, filing date22706950.704.02.2022
[2023/50]
WO2022US15294
Priority number, dateUS202163146383P05.02.2021         Original published format: US 202163146383 P
US202163185743P07.05.2021         Original published format: US 202163185743 P
US202163186491P10.05.2021         Original published format: US 202163186491 P
US202163283920P29.11.2021         Original published format: US 202163283920 P
[2023/50]
Filing languageEN
Procedural languageEN
PublicationType: A1 Application with search report
No.:WO2022170082
Date:11.08.2022
Language:EN
[2022/32]
Type: A1 Application with search report 
No.:EP4288556
Date:13.12.2023
Language:EN
The application published by WIPO in one of the EPO official languages on 11.08.2022 takes the place of the publication of the European patent application.
[2023/50]
Search report(s)International search report - published on:EP11.08.2022
ClassificationIPC:C12N15/864, A61K38/47, A61K48/00, C12N7/00
[2023/50]
CPC:
C12N15/86 (EP); A61K45/06 (EP); A61K48/005 (EP);
A61K48/0075 (EP); A61P3/00 (EP); A61P43/00 (EP);
C07K14/47 (EP); C12N9/16 (EP); C12N9/2402 (EP);
C12Y301/06013 (EP); C12Y302/01076 (EP); A61K38/00 (EP);
C12N2750/14143 (EP) (-)
Designated contracting statesAL,   AT,   BE,   BG,   CH,   CY,   CZ,   DE,   DK,   EE,   ES,   FI,   FR,   GB,   GR,   HR,   HU,   IE,   IS,   IT,   LI,   LT,   LU,   LV,   MC,   MK,   MT,   NL,   NO,   PL,   PT,   RO,   RS,   SE,   SI,   SK,   SM,   TR [2023/50]
TitleGerman:VERFAHREN ZUR PRÄVENTION VON HERZ- ODER SKELETTDEFEKTEN BEI KRANKHEITEN EINSCHLIESSLICH MUCOPOLYSACCHARIDOSEN[2023/50]
English:METHODS FOR PREVENTING CARDIAC OR SKELETAL DEFECTS IN DISEASES INCLUDING MUCOPOLYSACCHARIDOSES[2023/50]
French:MÉTHODES DE PRÉVENTION DE DÉFAUTS CARDIAQUES OU SQUELETTIQUES DANS DES MALADIES COMPRENANT DES MUCOPOLYSACCHARIDOSES[2023/50]
Entry into regional phase21.08.2023National basic fee paid 
21.08.2023Designation fee(s) paid 
21.08.2023Examination fee paid 
Examination procedure21.08.2023Examination requested  [2023/50]
21.08.2023Date on which the examining division has become responsible
17.04.2024Despatch of communication that the application is deemed to be withdrawn, reason: reply to the Extended European Search Report/Written Opinion of the International Searching Authority/International Preliminary Examination Report/Supplementary international search report not received in time
12.06.2024Amendment by applicant (claims and/or description)
Request for further processing for:12.06.2024Request for further processing filed
12.06.2024Full payment received (date of receipt of payment)
Request granted
14.06.2024Decision despatched
Fees paidRenewal fee
27.02.2024Renewal fee patent year 03
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Cited inInternational search[X]WO2014186579  (UNIV MINNESOTA [US]) [X] 1-26* p. 2, penultimate §-last §, p. 6, last §-p. 8, 1st §, , p. 14, penultimate §, p. 15, 1st §-2nd §, p. 2, last §, p. 4, penultimate §-last §, p. 3, 2nd §-3rd §, p. 20, 2nd §, p. 6, 2nd §, p. 20, 2nd §, p. 3, last §;; examples 1-2 *;
 [XI]WO2019010335  (UNIV PENNSYLVANIA [US]) [X] 1-21,23,25,26 * p. 9, 2nd §-3rd §, p. 11, 1st §-2nd §, p. 27, 1st §, p. 46, 2nd §, p. 47, 2nd §, p. 49, penultimate §-last §, p. 3, penultimate §, p. 28, last §, p. 16, 2nd §, p. 5, 1st §, p. 6, 2nd §, p. 50, 2nd §, p. 53, 2nd §-5th §, p. 7, last §, p. 16, 3rd §, p. 17, 3rd §, p. 43, penultimate §p. 51, last §, p. 10, penultimate §, p. 35, 3rd §-4th §, p. 16, 2nd §, p. 29, 2nd §;; examples 1-8 * [I] 22,24;
 [X]  - BELUR LALITHA ET AL, "Comparative systemic and neurologic effectiveness of intravenous and intrathecal AAV9 delivered individually or combined in a murine model of mucopolysaccharidosis type I", MOLECULAR GENETICS AND METABOLISM, ACADEMIC PRESS, AMSTERDAM, NL, vol. 132, no. 2, doi:10.1016/J.YMGME.2020.12.025, ISSN 1096-7192, (20210201), (20210201), XP086480758 [X] 1-10,13,15,16,18,20,21,23,25,26 * the whole document *

DOI:   http://dx.doi.org/10.1016/j.ymgme.2020.12.025
by applicantWO9413788
 WO9513392
 WO9617947
 US5656785
 US5658776
 WO9823018
 WO9827204
 WO2008049588
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