Extract from the Register of European Patents

EP Citations: EP1986661

Cited inSearch
Type:Non-patent literature
Publication information:[YD]   DODGE JAMES C ET AL: "Gene transfer of human acid sphingomyelinase corrects neuropathology and motor deficits in a mouse model of Niemann-Pick type A disease", PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA, vol. 102, no. 49, December 2005 (2005-12-01), pages 17822 - 17827, XP002671093, ISSN: 0027-8424 [YD] 14-19 * abstract * * page 17823 * * page 17822 *
DOI: http://dx.doi.org/10.1073/PNAS.0509062102
Type:Non-patent literature
Publication information:[YD]   PASSINI M A ET AL: "AAV Vector-Mediated Correction of Brain Pathology in a Mouse Model of Niemann-Pick A Disease", MOLECULAR THERAPY, ACADEMIC PRESS, SAN DIEGO, CA, US, vol. 11, no. 5, 1 May 2005 (2005-05-01), pages 754 - 762, XP004863183, ISSN: 1525-0016, DOI: 10.1016/J.YMTHE.2005.01.011 [YD] 14-19 * abstract * * page 761 * * page 754 *
DOI: http://dx.doi.org/10.1016/j.ymthe.2005.01.011
Type:Non-patent literature
Publication information:[Y]   BARBON ET AL: "AAV8-Mediated Hepatic Expression of Acid Sphingomyelinase Corrects the Metabolic Defect in the Visceral Organs of a Mouse Model of Niemann-Pick Disease", MOLECULAR THERAPY, ACADEMIC PRESS, SAN DIEGO, CA, US, vol. 12, no. 3, 1 September 2005 (2005-09-01), pages 431 - 440, XP005472377, ISSN: 1525-0016, DOI: 10.1016/J.YMTHE.2005.03.011 [Y] 14-19 * abstract * * page 438 - page 439 *
DOI: http://dx.doi.org/10.1016/j.ymthe.2005.03.011
Type:Non-patent literature
Publication information:[A]   "PARTICULARITIES OF LYSOSOMAL STORAGE DISEASES GENE THERAPY", GENE THERAPY, MACMILLAN PRESS LTD., BASINGSTOKE, GB, vol. 3, no. 12, 1 December 1996 (1996-12-01), pages 1039 - 1041, XP001007386, ISSN: 0969-7128 [A] 1-24 * page 1040 ff. *
Type:Non-patent literature
Publication information:[A]   JIN H-K ET AL: "Ex vivo gene therapy using bone marrow-derived cells: combined effects of intracerebral and intravenous transplantation in a mouse model of Niemann-Pick disease", MOLECULAR THERAPY, ACADEMIC PRESS, SAN DIEGO, CA, US, vol. 8, no. 6, 1 December 2003 (2003-12-01), pages 876 - 885, XP003002614, ISSN: 1525-0016 [A] 1-24 * abstract *
Type:Non-patent literature
Publication information:[T]   PASSINI MARCO A ET AL: "Combination brain and systemic injections of AAV provide maximal functional and survival benefits in the Niemann-Pick mouse", PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF USA, NATIONAL ACADEMY OF SCIENCE, WASHINGTON, DC; US, vol. 104, no. 22, 29 May 2007 (2007-05-29), pages 9505 - 9510, XP002455719, ISSN: 0027-8424, DOI: 10.1073/PNAS.0703509104 [T] * the whole document *
DOI: http://dx.doi.org/10.1073/pnas.0703509104
Cited inInternational search
Type:Patent literature
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Publication information:[X]   ELLIGER ET AL., MOLECULAR THERAPY, vol. 5, no. 5, 2002, pages 617 - 626, XP008090917
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Publication information:[Y]   OHASHI T. ET AL., PNAS, vol. 94, no. 4, 1997, pages 1287 - 1292, XP002122348
DOI: http://dx.doi.org/10.1073/pnas.94.4.1287
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Publication information:[A]   GONZALEZ-GOMEZ ET AL., AM. J. PATHOLOGY, vol. 153, no. 4, 1998, pages 1293 - 1300, XP008090668
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Publication information:[A]   AGUDO ET AL., HUMAN GENE THERAPY, vol. 13, no. 5, 20 March 2002 (2002-03-20), pages 665 - 674, XP003017729
DOI: http://dx.doi.org/10.1089/10430340252837251
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Publication information:[A]   VOLGER ET AL., J. INHER. METAB. DIS., vol. 21, 1998, pages 575 - 586, XP008091995
DOI: http://dx.doi.org/10.1023/A:1005423222927
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