EP2322618 - Methods for genetic modification of hematopoietic progenitor cells and uses of the modified cells [Right-click to bookmark this link] | Status | The application is deemed to be withdrawn Status updated on 21.06.2013 Database last updated on 13.07.2024 | Most recent event Tooltip | 21.06.2013 | Application deemed to be withdrawn | published on 24.07.2013 [2013/30] | Applicant(s) | For all designated states JOHNSON & JOHNSON RESEARCH PTY LIMITED Australian Technology Park Level 4 1 Central Avenue Eveleigh, NSW 1430 / AU | [2011/20] | Inventor(s) | 01 /
Symonds, Geoffrey P. 15 Hamilton Street Rosebay, NSW 2029 / AU | 02 /
Amado, Rafael 16050 Woodley Park Ln Encino, CA 91436 / US | 03 /
Sun, Lun-Quan 8 Banksia Street Eastwood, NSW 2122 / AU | 04 /
MacPherson, Janet 13 Day Street Leichhardt, NSW 2040 / AU | 05 /
Fanning, Greg 5/22 Read Street Bronte, NSW 2024 / AU | 06 /
Gerlach, Wayne 31 Barrie Street East Killara, NSW 2071 / AU | [2011/52] |
Former [2011/20] | 01 /
Symonds, Geoffrey P. 15 Hamilton Street Rosebay, NSW 2029 / AU | ||
02 /
Amado, Rafael 16050 Woodley Park Ln Encino, CA 91436 / US | |||
03 /
Sun, Lun-Quan 8 Banksia Street Eastwood, NSW 2122 / AU | |||
04 /
Macpherson, Janet 13 Day Street Leichhardt, NSW 2040 / AU | |||
05 /
Fanning, Greg 5/22 Read Street Bronte, NSW 2024 / AU | |||
06 /
Gerlach, Wayne 31 Barrie Street East Killara, NSW 2071 / AU | Representative(s) | Sellin, Carole, et al Ernest Gutmann - Yves Plasseraud S.A.S 88, Boulevard des Belges 69452 Lyon Cedex 06 / FR | [2011/20] | Application number, filing date | 10183035.4 | 10.07.2002 | [2011/20] | Priority number, date | US20010304127P | 10.07.2001 Original published format: US 304127 P | US20010304283P | 10.07.2001 Original published format: US 304283 P | US20010343484P | 21.12.2001 Original published format: US 343484 P | US20020386063P | 04.06.2002 Original published format: US 386063 P | [2011/20] | Previously filed application, date | WO2002US21907 | 10.07.2002 | [2011/20] | Filing language | EN | Procedural language | EN | Publication | Type: | A1 Application with search report | No.: | EP2322618 | Date: | 18.05.2011 | Language: | EN | [2011/20] | Search report(s) | (Supplementary) European search report - dispatched on: | EP | 14.04.2011 | Classification | IPC: | C12N15/113, A61K31/7105, A61K35/12 | [2011/20] | CPC: |
C12N15/1132 (EP,US);
A61K48/00 (EP,KR,US);
A61P31/18 (EP);
A61K2035/124 (EP,US);
A61K38/00 (EP,US);
C12N2310/111 (EP,US);
| Designated contracting states | AT, BE, BG, CH, CY, CZ, DE, DK, EE, ES, FI, FR, GB, GR, IE, IT, LI, LU, MC, NL, PT, SE, SK, TR [2011/20] | Title | German: | Verfahren zur genetischen Modifikation von hämatopoetischen Vorläuferzellen und Verwendungen der modifizierten Zellen | [2011/20] | English: | Methods for genetic modification of hematopoietic progenitor cells and uses of the modified cells | [2011/20] | French: | Procédés de modification génétique des cellules progénitrices hématopoïétiques et utilisation des cellules modifiées | [2011/20] | Examination procedure | 18.11.2011 | Examination requested [2011/52] | 07.03.2012 | Amendment by applicant (claims and/or description) | 01.02.2013 | Application deemed to be withdrawn, date of legal effect [2013/30] | 11.02.2013 | Despatch of a communication from the examining division (Time limit: M04) | 11.03.2013 | Despatch of communication that the application is deemed to be withdrawn, reason: renewal fee not paid in time [2013/30] | Parent application(s) Tooltip | EP02746963.4 / EP1414996 | Divisional application(s) | The date of the Examining Division's first communication in respect of the earliest application for which a communication has been issued (EP20020746963) is 08.08.2007 | Request for further processing for: | The application is deemed to be withdrawn due to failure to reply to the Extended European Search Report/Written Opinion of the International Searching Authority/International Preliminary Examination Report/Supplementary international search report/Supplementary European search report | 07.03.2012 | Request for further processing filed | 07.03.2012 | Full payment received (date of receipt of payment) Request granted | 22.03.2012 | Decision despatched | Fees paid | Renewal fee | 28.01.2011 | Renewal fee patent year 03 | 28.01.2011 | Renewal fee patent year 04 | 28.01.2011 | Renewal fee patent year 05 | 28.01.2011 | Renewal fee patent year 06 | 28.01.2011 | Renewal fee patent year 07 | 28.01.2011 | Renewal fee patent year 08 | 28.01.2011 | Renewal fee patent year 09 | 30.01.2012 | Renewal fee patent year 10 | Penalty fee | Additional fee for renewal fee | 31.07.2011 | 10   M06   Fee paid on   30.01.2012 | 31.07.2012 | 11   M06   Not yet paid |
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Responsibility for the accuracy, completeness or quality of the data displayed under the link provided lies entirely with the Unified Patent Court. | Documents cited: | Search | [XI] - AMADO R ET AL, "A phase I gene therapy clinical study of autologous CD34+ cells transduced with an anti-HIV-1 ribozyme", BLOOD, AMERICAN SOCIETY OF HEMATOLOGY, US, (19981115), vol. 92, no. 10 SUPPL. 1 PART 1-2, ISSN 0006-4971, page 665A, XP002407451 [X] 1-4,6-11,13 * the whole document * [I] 1-14 | Examination | WO0075291 | - Cowan ET AL, "Paclitaxel chemotherapy after autologous stem-cell transplantation and engraftment of hematopoietic cells transduced with a retrovirus containing the multidrug resistance complementary DNA (MDR1) in metastatic breast cancer patients.", Clinical Cancer Research, (19990701), vol. 5, no. 7, ISSN 1078-0432, pages 1619 - 1628, XP055050456 | - HUHN R D ET AL, "Retroviral marking and transplantation of rhesus hematopoietic cells by nonmyeloablative conditioning.", HUMAN GENE THERAPY 20 JUL 1999, (19990720), vol. 10, no. 11, ISSN 1043-0342, pages 1783 - 1790 | - DUNBAR C E ET AL, "Retroviral transfer of the glucocerebrosidase gene into CD34+ cells from patients with Gaucher disease: in vivo detection of transduced cells without myeloablation.", HUMAN GENE THERAPY 20 NOV 1998, (19981120), vol. 9, no. 17, ISSN 1043-0342, pages 2629 - 2640 | by applicant | US5856188 | US6127114 | US6221661 | - ABONOUR ET AL., NATURE MEDICINE, (2000), vol. 6, pages 552 - 8 | - AMADO ET AL., HUMAN GENE THER, (1998), vol. 9, pages 173 - 183 | - AMADO; CHEN, SCIENCE, (1999), vol. 285, pages 674 - 676 | - AMADO ET AL., HUMAN GENE THER, (1999), vol. 10, pages 2255 - 2270 | - AUSTIN ET AL., BLOOD, (2000), vol. 95, pages 829 - 36 | - AUTRAN ET AL., SCIENCE, (1997), vol. 277, pages 112 - 116 | - BAGNIS ET AL., EXP HEMATOL, (2002), vol. 30, pages 108 - 15 | - BAI ET AL., MOLECULAR THERAPY, (2000), vol. 1, pages 244 - 54 | - BARNETT ET AL., BRIT J HEMATOL, (1998), vol. 102, pages 553 - 65 | - BAZIN ET AL., BIOCHEM PHARMACOL, (1989), vol. 38, pages 109 - 19 | - BEHRINGER ET AL., BONE MARROW TRANSPLANT, (1999), vol. 24, pages 295 - 302 | - BENBOUBKER ET AL., BRIT J HEMATOL, (2001), vol. 113, pages 247 - 50 | - BENDER ET AL., J VIROL, (1987), vol. 61, pages 1639 - 46 | - BENDER ET AL., BLOOD, (1991), vol. 77, pages 2591 - 6 | - BERTOLINI ET AL., BONE MARROW TRANSPLANT, (1998), vol. 21, pages 5 - 7 | - BODINE ET AL., ANN NY ACAD SCI, (1998), vol. 850, pages 139 - 50 | - BONYHADI ET AL., J VIROL, (1997), vol. 71, pages 4704 - 16 | - BORDIGNON ET AL., SCIENCE, (1995), vol. 270, pages 470 - 5 | - BRENNER, J INT MEDICINE, (2001), vol. 249, pages 345 - 58 | - BRIONES ET AL., HAEMATOLOGICA, (1999), vol. 84, pages 483 - 8 | - BROOKS ET AL., NATURE MED, (2001), vol. 7, pages 459 - 64 | - BUNNELL; MORGAN, CLIN MICRO REV, (1998), vol. 11, pages 42 - 56 | - BUNTING ET AL., ANN NY ACAD SCI, (1999), vol. 872, pages 125 - 40 | - CAMPOS, LEUKEMIA, (1993), vol. 7, pages 1409 - 15 | - CASE ET AL., PROC NATL ACAD SCI USA, (1999), vol. 96, pages 2988 - 93 | - CARPINTEIRO ET AL., INT J OF CANCER, (2002), vol. 98, pages 785 - 92 | - CAVAZZANA-CALVO ET AL., SCIENCE, (2000), vol. 288, pages 669 - 672 | - CAVAZZANA-CALVO, J GENE MED, (2001), vol. 3, pages 201 - 6 | - CHALLITA; KOHN, PROC NATL ACAD SCI USA, (1994), vol. 91, pages 2567 - 71 | - CHANG; RONINSON, GENE, (1996), vol. 183, pages 137 - 42 | - CHATTERJEE ET AL., BLOOD, (1999), vol. 93, pages 1882 - 1894 | - CHENG ET AL., NAT MED, (2000), vol. 6, pages 1235 - 40 | - CHERRY ET AL., MOL CELL BIOL, (2000), vol. 20, pages 7419 - 26 | - CHU ET AL., J MOL MED, (1998), vol. 76, pages 184 - 192 | - COHEN-HAGUENAUER ET AL., HUM GENE THER, (1998), vol. 9, pages 207 - 16 | - COMETTA ET AL., HUM GENE THER, (1996), vol. 7, pages 1323 - 30 | - CRYSTAL, SCIENCE, (1995), vol. 270, pages 404 - 10 | - DAO ET AL., BLOOD, (1997), vol. 89, pages 446 - 56 | - DAO ET AL., PROC NATL ACAD SCI USA, (1998), vol. 95, pages 13006 - 11 | - DAO ET AL., BLOOD, (1998), vol. 92, pages 4612 - 21 | - DAO; NOLTA, LEUKEMIA, (1999), vol. 13, pages 1473 - 80 | - DAO; NOLTA, LEUKEMIA, (2000), vol. 14, pages 773 - 6 | - DONAHUE ET AL., NATURE MED, (1998), vol. 4, pages 181 - 6 | - DOUEK ET AL., NATURE, (1998), vol. 396, pages 690 - 695 | - DUCOS ET AL., GENE THER, (2000), vol. 7, pages 1790 - 4 | - DUNBAR ET AL., BLOOD, (1995), vol. 85, pages 3048 - 3057 | - DUNBAR ET AL., HUM GENE THER, (1998), vol. 9, pages 2629 - 40 | - DUNBAR ET AL., HUM GENE THER, (1998), vol. 7, pages 231 - 53 | - DUNBAR ET AL., ANN NY ACAD SCI, (2001), vol. 938, pages 236 - 45 | - EGLITIS; SCHNEIDERMAN, BIOCHEM BIOPHYS RES COMMUN, (1997), vol. 231, pages 477 - 80 | - FAN ET AL., HUM GENE THER, (2000), vol. 11, pages 1313 - 27 | - FEHSE ET AL., HUM GENE THER, (1997), vol. 8, pages 1815 - 24 | - FENG ET AL., NATURE BIOTECHNOL, (1997), vol. 15, pages 866 - 870 | - FISHER-ADAMS ET AL., BLOOD, (1996), vol. 88, pages 492 - 504 | - FU; LIESVELD, BLOOD REV, (2000), vol. 14, pages 205 - 18 | - GABARRE ET AL., THE LANCET, (2000), vol. 355, pages 1071 - 2 | - GAMBOTTO ET AL., METHODS MOL BIOL, (2000), vol. 135, pages 495 - 508 | - GERARD ET AL., HUM GENE THER, (1996), vol. 7, pages 343 - 54 | - GERVAIX ET AL., HUM GENE THER, (1997), vol. 8, pages 2229 - 38 | - GIARRATANA ET AL., BONE MARROW TRANSPL, (1998), vol. 22, pages 707 - 15 | - GLIMM ET AL., HUM GENE THER, (1998), vol. 9, pages 771 - 8 | - GLUCKMAN, EXP HEMATOL, (2000), vol. 28, pages 1197 - 205 | - GOERNER ET AL., BLOOD, (1999), vol. 94, pages 2287 - 92 | - GOTHOT ET AL., BLOOD, (1998), vol. 92, pages 2641 - 2649 | - GRANDE ET AL., BLOOD, (1999), vol. 93, pages 3276 - 85 | - GRIMM; KLEINSCHMIDT, HUM GENE THER, (1999), vol. 10, pages 2445 - 2450 | - HAAS ET AL., MOL THER, (2000), vol. 2, pages 71 - 80 | - HACEIN-BEY-ABINA ET AL., NEW ENG J MEDICINE, (2002), vol. 346, pages 1185 - 93 | - HALENE ET AL., BLOOD, (1999), vol. 94, pages 3349 - 57 | - HALENE; KOHN, HUM GENE THER, (2000), vol. 11, pages 1259 - 67 | - HAMPEL ET AL., NUCLEIC ACIDS RES, (1990), vol. 18, pages 299 - 304 | - HANENBERG ET AL., NAT MED, (1996), vol. 2, pages 876 - 82 | - HANENBERG ET AL., HUM GENE THER, (1997), vol. 8, pages 2193 - 2206 | - HAO ET AL., BLOOD, (1996), vol. 88, pages 3306 - 3313 | - HARRISON, BLOOD, (1980), vol. 55, pages 77 - 81 | - HARRISON ET AL., PROC NATL ACAD SCI USA, (1988), vol. 85, pages 822 - 6 | - HASELOFF; GERLACH, NATURE, (1988), vol. 334, pages 585 - 91 | - HENNEMANN ET AL., EXP HEMATOL, (1999), vol. 27, pages 817 - 825 | - HERRERA ET AL., BRIT J HEMATOL, (2001), vol. 114, pages 920 - 30 | - HESFORFFER ET AL., J CLIN ONCOL, (1998), vol. 16, pages 165 - 72 | - HO, LEUKEMIA, (1993), vol. 7, pages 1738 - 46 | - HO ET AL., NATURE, (1995), vol. 373, pages 123 - 126 | - HO ET AL., BLOOD, (1996), vol. 88, no. 1, page 405 | - HODGSON; BRADLEY, NATURE, (1979), vol. 281, pages 381 - 2 | - HOGAN ET AL., PROC NATL ACAD SCI USA, (2002), vol. 99, pages 413 - 8 | - HOOGERBRUGGE ET AL., GENE THER, (1996), vol. 3, pages 179 - 183 | - HUHN ET AL., EXP HEMATOL, (1996), vol. 24, pages 839 - 47 | - HUSS, STEM CELLS, (2000), vol. 18, pages 1 - 9 | - HUTCHINGS ET AL., J HEMATOTHER, (1998), vol. 7, pages 217 - 24 | - IMBERT ET AL., EXP HEMATOL, (1998), vol. 26, pages 374 - 81 | - JAMIESON ET AL., IMMUNITY, (1999), vol. 10, pages 569 - 575 | - JONES ET AL., NATURE, (1990), vol. 347, pages 188 - 9 | - KANSAS, BLOOD, (1996), vol. 88, pages 3259 - 87 | - KIEM ET AL., BLOOD, (1997), vol. 90, pages 4638 - 4645 | - KIEM ET AL., BLOOD, (1998), vol. 92, pages 1878 - 1886 | - KIRBY ET AL., BLOOD, (2000), vol. 95, pages 3710 - 5 | - KNAAN-SHANZER ET AL., HUM GENE THER, (2001), vol. 12, pages 1989 - 2005 | - KNOP ET AL., GENE THERAPY, (1999), vol. 6, pages 373 - 84 | - KOBARI ET AL., EXP HEMATOL, (2000), vol. 28, pages 1470 - 80 | - KOHN, NATURE MEDICINE, (1995), vol. 1, pages 1017 - 1023 | - KOHN ET AL., NATURE MEDICINE, (1998), vol. 4, pages 775 - 780 | - KOHN ET AL., BLOOD, (1999), vol. 94, pages 368 - 71 | - KRAMER ET AL., PROC NATL ACAD SCI USA, (1999), vol. 96, pages 2087 - 92 | - KUME ET AL., INT J HEMATOL, (1999), vol. 69, pages 227 - 33 | - LANE ET AL., BLOOD, (1995), vol. 85, pages 275 - 82 | - LANGE; BLANKENSTEIN, GENE THERAPY, (1997), vol. 4, pages 303 - 8 | - LATAILLADE ET AL., BLOOD, (2000), vol. 95, pages 756 - 68 | - LAW ET AL., EXP HEMATOL, (1999), vol. 27, pages 147 - 54 | - LEDOUX ET AL., HUM GENE THER, (2001), vol. 12, pages 1611 - 21 | - LEE ET AL., J VIROL, (1994), vol. 68, pages 8254 - 64 | - LEWIS; VERFAILLIE, EXP HEMATOL, (2000), vol. 28, pages 1087 - 95 | - LIEBER ET AL., J VIROL, (1999), vol. 73, pages 9314 - 24 | - LISZIEWICZ ET AL., PROC NATL ACAD SCI USA, (1993), vol. 90, pages 8000 - 4 | - LIU ET AL., HUM GENE THER, (1999), vol. 10, pages 2337 - 46 | - LYMAN; JACOBSEN, BLOOD, (1998), vol. 91, pages 1101 - 34 | - MACIEJEWSKI ET AL., NATURE MED, (1995), vol. 1, pages 667 - 73 | - MALECH ET AL., PROC NATL ACAD SCI USA, (1997), vol. 94, pages 12133 - 8 | - MALIK ET AL., BLOOD, (1995), vol. 86, pages 2993 - 3005 | - MARANDIN ET AL., BLOOD, (1996), vol. 88, pages 4568 - 78 | - MARASCO ET AL., HUMAN GENE THER, (1998), vol. 9, pages 1627 - 42 | - MARINI ET AL., CANER GENE THER, (2000), vol. 7, pages 816 - 25 | - MARTINEZ ET AL., EXP HEMATOL, (1999), vol. 27, pages 561 - 8 | - MAUTINO; MORGAN, AIDS PATIENT CARE AND STDS, (2002), vol. 16, pages 11 - 26 | - MICHALLET ET AL., EXP HEMATOL, (2000), vol. 28, pages 858 - 70 | - MICHIENZI ET AL., PROC NATL ACAD SCI USA, (2000), vol. 97, pages 8955 - 60 | - MILLER; BUTTIMORE, MOL CELL BIOL, (1986), vol. 6, pages 2895 - 902 | - MIYOSHI ET AL., SCIENCE, (1999), vol. 283, pages 682 - 686 | - MOORE; MACKENZIE, PROG EXP TUMOR RES, (1999), vol. 36, pages 20 - 49 | - MOUNTAIN, TIBTECH, (2000), vol. 18, pages 119 - 128 | - MURRAY ET AL., EXP HEMATOL, (1999), vol. 27, pages 1019 - 28 | - MURRAY ET AL., HUM GENE THER, (2000), vol. 11, pages 2039 - 50 | - NAGLER ET AL., EXP HEMATOL, (2000), vol. 28, pages 1096 - 104 | - NALDINI ET AL., SCIENCE, (1996), vol. 272, pages 263 - 7 | - NEWBOUND ET AL., EXP HEMATOL, (2001), vol. 29, pages 163 - 73 | - NG ET AL., BRIT J HEMATOL, (2002), vol. 117, pages 226 - 37 | - NOLTA ET AL., EXP HEMATOL, (1992), vol. 20, pages 1065 - 1071 | - OGAWA ET AL., BLOOD, (1993), vol. 81, pages 2844 - 2853 | - OJWANG ET AL., PROC NATL ACAD SCI USA, (1992), vol. 89, pages 10802 - 6 | - OMORI ET AL., J HEMATOTHER STEM CELL RES, (1999), vol. 8, pages 503 - 14 | - ORLIC; BODINE, BLOOD, (1994), vol. 84, pages 3991 - 3994 | - ORLIC ET AL., ANN NY ACAD SCI, (1999), vol. 872, pages 115 - 24 | - ORLIC ET AL., ANN NY ACAD SCI, (2001), vol. 938, pages 221 - 230 | - OSTROWSKI ET AL., J VIROL, (1999), vol. 73, pages 6430 - 5 | - QUAN ET AL., EXP HEMATOL, (1999), vol. 27, pages 1511 - 8 | - PAKKER ET AL., NATURE MEDICINE, (1998), vol. 4, pages 208 - 14 | - PARKMAN, SCIENCE, (1986), vol. 232, pages 1373 - 78 | - PETERS ET AL., BLOOD, (1996), vol. 87, pages 30 - 7 | - PICKER ET AL., J IMMUNOL, (1993), vol. 150, pages 1105 - 21 | - POULIN ET AL., J EXP MED, (1999), vol. 190, pages 479 - 86 | - RAGG ET AL., CANCER RES, (2000), vol. 60, pages 5187 - 95 | - RAMEZANI ET AL., FRONTIERS IN BIOSCIENCE, (2002), vol. 7, pages A29 - 36 | - RANGA ET AL., PROC NATL ACAD SCI USA, (1998), vol. 95, pages 1201 - 6 | - REESE ET AL., J HEMATOTHER STEM CELL RES, (1999), vol. 8, pages 515 - 23 | - REIS, TRANSPLANT PROC, (1999), vol. 31, pages 2970 - 2 | - RELANDER ET AL., J GENE MED, (2001), vol. 3, pages 207 - 18 | - RELANDER ET AL., J GENE MED, (2002), vol. 4, pages 122 - 32 | - RICHTER; KARLSON, INT J HEMATOL, (2001), vol. 73, pages 162 - 69 | - RIVELLA ET AL., J VIROLOGY, (2000), vol. 74, pages 4679 - 87 | - ROBBINS ET AL., PROC NATL ACAD SCI USA, (1998), vol. 95, pages 10182 - 7 | - ROE ET AL., EMBO J, (1993), vol. 12, pages 2099 - 2108 | - ROSLER ET AL., EXP HEMATOL, (2000), vol. 28, pages 841 - 52 | - ROSSI ET AL., AIDS RES AND HUMAN RETROVIRUSES, (1992), vol. 8, pages 183 - 9 | - ROVIRA ET AL., BLOOD, (2000), vol. 96, pages 4111 - 7 | - SADELAIN ET AL., CURR OPIN HEMATOL, (2000), vol. 7, pages 364 - 77 | - SANDERS ET AL., IMMUNOL TODAY, (1988), vol. 9, pages 195 - 9 | - SANDHAUS ET AL., EXP HEMATOL, (1998), vol. 26, pages 73 - 8 | - SANYAL; SCHUENING, HUM GENE THER, (1999), vol. 10, pages 2859 - 68 | - SARVER ET AL., SCIENCE, (1990), vol. 247, pages 1222 - 5 | - SATO ET AL., BLOOD, (1999), vol. 94, pages 2548 - 2554 | - SAYLORS ET AL., GENE THER, (1999), vol. 6, pages 944 - 6 | - SCHILZ ET AL., BLOOD, (1998), vol. 92, pages 3163 - 71 | - SCHILZ ET AL., MOL THER, (2000), vol. 2, pages 609 - 18 | - SCHILZ ET AL., J GENE MED, (2001), vol. 3, pages 427 - 36 | - SCZAKIEL; PAWLITA, J VIROL, (1991), vol. 65, pages 468 - 72 | - SHAHEEN ET AL., J VIROL, (1996), vol. 70, pages 3392 - 400 | - SIENA ET AL., BLOOD, (1989), vol. 74, pages 1905 - 14 | - SMYTHE ET AL., PROC NATL ACAD SCI USA, (1994), vol. 91, pages 3657 - 61 | - SOLAR ET AL., BLOOD, (1998), vol. 92, pages 4 - 10 | - STRAYER ET AL., GENE THER, (2000), vol. 7, pages 886 - 95 | - SU ET AL., BLOOD, (1997), vol. 89, pages 2283 - 90 | - SUN ET AL., PROC NATL ACAD SCI USA, (1995), vol. 92, pages 7272 - 6 | - SUN ET AL., NUCL ACIDS RESEARCH, (1995), vol. 23, pages 2909 - 13 | - SUN ET AL., NUCL ACIDS MOL BIOL CATALYTIC RNA, (1996), vol. 10, pages 329 - 342 | - SUTTON ET AL., J VIROL, (1998), vol. 72, pages 5781 - 8 | - TAKATOKU ET AL., J CLINICAL INVESTIG, (2001), vol. 108, pages 447 - 55 | - TAKENAKA ET AL., PNAS, (2000), vol. 97, pages 7515 - 20 | - TAKIYAMA ET AL., EUR J HEMATOL, (1998), vol. 61, pages 1 - 6 | - TAVOLINI, GENE THER, (1997), vol. 4, pages 150 - 5 | - THOMAS ET AL., METHODS, (1999), vol. 17, pages 202 - 18 | - TO ET AL., BLOOD, (1997), vol. 85, pages 2233 - 58 | - TRAYCOFF ET AL., EXP HEMATOL, (1998), vol. 26, pages 53 - 62 | - UCHIDA ET AL., PROC NATL ACAD SCI USA, (1998), vol. 95, pages 1939 - 44 | - VASSILOPOULOS ET AL., BLOOD, (2001), vol. 98, pages 604 - 609 | - VERES ET AL., J VIROL, (1998), vol. 72, page 1894 | - VERFAILLIE ET AL., EXP HEMATOL, (2000), vol. 28, pages 1071 - 9 | - VIGNOLI ET AL., AIDS, (1998), vol. 12, pages 999 - 1005 | - VON LAER ET AL., J VIROL, (1998), vol. 72, pages 1424 - 30 | - WANG ET AL., HUMAN GENE THER, (1998), vol. 9, pages 1283 - 91 | - WARD ET AL., AMERICAN J PATHOLOGY, (1998), vol. 153, pages 373 - 379 | - WILCOX ET AL., BLOOD, (2000), vol. 95, pages 3645 - 52 | - WILLIAMS ET AL., ANN NY ACAD SCI, (1999), vol. 872, pages 109 - 13 | - YU ET AL., PROC NATL ACAD SCI USA, (1995), vol. 92, pages 699 - 703 | - ZANJANI ET AL., EXP HEMATOL, (1998), vol. 26, pages 353 - 60 | - ZAULI ET AL., J EXP MED, (1996), vol. 183, pages 99 - 108 | - ZHANG ET AL., J EXP MED, (1999), vol. 190, pages 725 - 32 | - ZHANG ET AL., PROC NATL ACAD SCI USA, (1998), vol. 95, pages 1154 - 9 | - ZIMMERMANN ET AL., BONE MARROW TRANSPL, (1995), vol. 9, pages 439 - 44 | US20010304127 | US20010304283 | US20010343484 | US20020386063 |